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Rare and heterogeneous manifestations of leucocyte adhesion deficiency type 1: report of two cases with diagnostic dilemmas and novel ITGB2 mutation

2nd International Conference on Pediatrics & Neonatology

March 20, 2025 | Virtual Event

Sabahat Sarfaraz

Dow University of Health Sciences, Pakistan

Abstract :

Primary immunodeficiency disorders (PID) are rare disorders with heterogeneous manifesta­tions, overlapping with other diseases such as autoimmunity, malignancy, and infections. This makes the diagnosis very challenging and delays management. Leucocyte adhesion defects (LAD) are a group of PIDs in which patients lack adhesion molecules on leukocytes needed for their emigration through blood vessels to the site of infection. Patients with LAD can pres­ent with diverse clinical features including severe and life-threatening infections, early in life, and the absence of pus formation around infection or inflammation. There is often delayed umbilical cord separation, omphalitis, late wound healing, and a high white blood cell count. If not recognized and managed early, can lead to life-threatening complications and death.

Case Presentation: LAD 1 is characterized by homozygous pathogenic variants in the inte­grin subunit beta 2 (ITGB2) gene. We report two cases of LAD1 with unusual presentations (post-circumcision excessive bleeding and chronic inflammation of the right eye) which were confirmed by flow cytometric analysis and genetic testing. We found two disease-causing ITGB2 pathogenic variants in both cases.

Conclusions: These cases highlight the importance of a multidisciplinary approach to recog­nizing clues in patients with uncommon manifestations of a rare disease. This approach ini­tiates a proper diagnostic workup of primary immunodeficiency disorder leading to a better understanding of the disease, and appropriate patient counseling, and helps clinicians to be better equipped to deal with complications.

Biography :

Sabahat Sarfaraz is an Assistant Professor of Pathology at Dow International Medical College, and Dow Uni­versity of Health Sciences. She has a keen interest in allergy diagnosis and testing. Besides she runs a transplant immunology lab at DUHS.